Empirical and Computational Comparison of Alternative Therapeutic Exon Skip Repairs for Duchenne Muscular Dystrophy
K. M. Ma, E. S. Thomas, J. Wereszczynski, N. Menhart
The paper compares alternative exon skip repairs for Duchenne muscular dystrophy, finding stability differences between edits and identifying structural perturbations as the cause.
bioRxiv · Jan 24, 2019Biophysics