Fully Personalised Degenerative Disease Modelling - A Duchenne Muscular Dystrophy Case Study
Evan Baker, Peter Challenor, Ian Bamsey, Francesco Muntoni A, Adnan Yousaf Manzur, Krasimira T. Tsaneva-Atanasova
The paper presents a framework for predicting individual patient trajectories in degenerative diseases using mixed data from the patient and a database, showing promising results in Duchenne Muscular Dystrophy.
medRxiv · Jul 28, 2022 · PreprintGenetic & Genomic Medicine