Assessment of CSF biomarkers and microRNA-mediated disease mechanisms in SMA
Emily Welby, Rebecca Rehborg, Matthew M. Harmelink, Allison D. Ebert
This study assesses CSF biomarkers and microRNA-mediated mechanisms in SMA patients treated with nusinersen, finding improved microRNA expression but persistent cellular stress and astrocyte dysfunction.
bioRxiv · May 19, 2021 · PreprintNeuroscience