Molecular BiologybioRxivPreprint
CFTR corrector efficacy is associated with occupancy of distinct binding sites
Nesrine Baatallah, Ahmad Elbahnsi, Jean‐Paul Mornon…·Alexandre Hinzpeter
The paper identifies two distinct VX-809 binding sites on CFTR that are critical for corrector efficacy, showing different sensitivity to mutations and allostery.
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