Adjunctive nebulization of Idursulfase to intravenous treatment enhances cardiac proteome adaptations in IDS-KO mice
Vinicius M. Mariani, Anatália Labilloy, W. Todd Cade, Paulo R. Ferreira, Leonardo F. Ferreira
This study compares proteomic changes in IDS-KO mice treated with IV and adjunct nebulized Idursulfase, finding that nebulization enhances cardiac proteome adaptations.
bioRxiv · Sep 10, 2026 · PreprintCell Biology