GeneticsbioRxivPreprint
Empirical Simulation and In Silico Evaluation of an Ethically Governed, AI-Enhanced CRISPR Prime Editing Framework for TOR1A Mutation Correction in Dystonia
Grace M. Thiong’o, Adegboyega Ogundokun
The paper develops an AI-enhanced CRISPR prime editing framework for correcting TOR1A mutations in dystonia, showing strong predictive performance and identifying key factors influencing editing efficiency.
DOI 10.1101/2025.04.22.650096