Arrayed CRISPR/Cas9 Loss-Of-Function Screen in a Neuronal Model of Adaptor Protein Complex 4 Deficiency Identifies Modulators of ATG9A Trafficking
Marvin Ziegler, Cedric Böger, Julian E. Alecu, Hyo‐Min Kim, Afshin Saffari, Alexandra K. Davies, Mustafa Şahin, Darius Ebrahimi‐Fakhari
The paper uses a CRISPR/Cas9 screen to identify genes modulating ATG9A trafficking in a neuronal model of AP-4 deficiency, revealing ANPEP and NPM1 as key regulators.
bioRxiv · Feb 22, 2025 · PreprintCell Biology