NeuroscienceStem Cell ReportsPeer-reviewed
Human motor units in microfluidic devices are impaired by FUS mutations and improved by HDAC6 inhibition
Katarina Stoklund Dittlau, Emily N. Krasnow, Laura Fumagalli…·Ludo Van Den Bosch
This study uses a microfluidic model of human motor units to show that FUS mutations impair neurite outgrowth and NMJ formation, which can be mitigated by HDAC6 inhibition.
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