Characteristics and data reporting of rare disease clinical trials: Getting better but still room for improvement
N. K. Mair, J. Gottowik, R. Rodriguez-Esteban, T. J. Seabrook
This paper analyzes rare disease clinical trials, finding that while some improvements have been made, result reporting remains inadequate, with many trials not disclosing results on ClinicalTrials.gov.
bioRxiv · Dec 3, 2021 · PreprintScientific Communication & Education