Unbiased human genomic characterization of polyglutamine disorder genes to guide biological understanding and therapeutic strategies
Kevin Lucy Namuli, Britt I. Drögemöller, Galen E.B. Wright
This study identifies potential adverse effects of knocking down polyQ disorder genes using genomic data and highlights risks for drug targeting.
Human Genetics and Genomics Advances · Nov 20, 2025Peer-reviewedGenetic & Genomic Medicine