AAV Capsid Screening for Translational Pig Research Using a Mouse Xenograft Liver Model
Melanie Willimann, Amita Tiyaboonchai, Kei Adachi, Bin Li, Lea Waldburger, Hiroyuki Nakai, Markus Grompe, Beat Thöny
The paper evaluates AAV capsids for liver gene therapy in a pig xenograft model, identifying efficient capsids for transgene expression in porcine hepatocytes.
bioRxiv · May 29, 2024 · PreprintMolecular Biology