Utilization of CoRDS Registry to Monitor Quality of Life in Patients with VCP Multisystem Proteinopathy
Eiman Abdoalsadig, Merwa Hamid, Allison Peck, Leepakshi Johar, Virginia E. Kimonis
This study uses the CoRDS registry to track quality of life in VCP disease patients, finding significant declines in mobility and function over time.
Orphanet Journal of Rare Diseases · Apr 14, 2025Peer-reviewedGenetic & Genomic Medicine