Transgenic mice expressing tunable levels of DUX4 develop characteristic facioscapulohumeral muscular dystrophy-like pathophysiology ranging in severity
T. I. Jones, G.-L. Chew, P. Barraza-Flores, S. Schreier, M. Ramirez, R. D. Wuebbles, D. J. Burkin, R. K. Bradley, P. L. Jones
This paper develops a bi-transgenic mouse model that allows controlled expression of DUX4 to study FSHD-like pathophysiology with varying severity.
Skeletal Muscle · Apr 11, 2020Peer-reviewedCell Biology