Genetically engineered microglia-like cells have therapeutic potential for neurodegenerative disease
Robert N. Plasschaert, Mark P. DeAndrade, Fritz Hull, Quoc Nguyen, Tara Peterson, Aimin Yan, Mariana Loperfido, Cristina Baricordi, Luigi Barbarossa, John K. Yoon, Yildirim Dogan, Zeenath Unnisa, Jeffrey W. Schindler, Niek Peter van Til, Luca Biasco, Chris Mason
This study shows genetically engineered microglia-like cells can provide therapeutic protein levels in mouse models of neurodegenerative diseases.
bioRxiv · Sep 16, 2021 · PreprintNeuroscience