Deletion of miR-146a enhances therapeutic protein restoration in model of dystrophin exon skipping
Nikki M. McCormack, Kelsey A. Calabrese, Christina M. Sun, Christopher Tully, Christopher R. Heier, Alyson A. Fiorillo
The paper shows that deleting miR-146a enhances dystrophin protein restoration in a DMD model using exon skipping therapy.
Molecular Therapy — Nucleic Acids · May 24, 2024Peer-reviewedMolecular Biology