GeneticsJournal of Cachexia Sarcopenia and MusclePeer-reviewed
Cholesterol metabolism is a potential therapeutic target in Duchenne Muscular Dystrophy
Fatima Amor, Ai Vu Hong, Guillaume Corre…·David Israeli
This study identifies dysregulated miRNAs in DMD patients and mice, linking cholesterol metabolism and the mevalonate pathway to disease progression, with Simvastatin treatment showing therapeutic potential.