Pharmacology & ToxicologyScientific ReportsPeer-reviewed
Identification of compounds that repress DUX4 expression in facioscapulohumeral muscular dystrophy
Ning Chang, Hannah P. Moore, Charis L. Himeda…·Peter L. Jones
This study identifies a compound, C06, that effectively represses DUX4 expression in FSHD myocytes using AI-based screening and validation.
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