Astrocyte targeted SMN1 gene therapy and forskolin application improves astrocyte filopodia actin defects and motor neuron synaptic dysfunction in human SMA disease pathology
Emily Welby, Xiaojie Liu, Melinda S. Wojtkiewicz, Linda Berg Luecke, Rebekah L. Gundry, Qingsong Liu, Allison D. Ebert
bioRxiv · Mar 27, 2026 · PreprintNeuroscience