A NEW DYSTROPHIN DEFICIENT RAT MODEL MIRRORING EXON SKIPPING IN PATIENTS WITH DMD EXON 45 DELETIONS
Tao Wang, Cynthia Daoud, Auriane Dubois, Guillaume Corre, Jessica Bellec, Matteo Bovolenta, Louise Philidet, Alan Dorval, Nathalie Bourg, Carinne Roudaut, Sonia Albini, Ganesh Warthi, Abbass Jaber, Isabelle Richard
This paper describes a novel rat model with an exon 45 deletion in the Dmd gene, showing features of DMD and exon skipping, which may inform personalized therapies.
Disease Models & Mechanisms · Jan 1, 2026Peer-reviewedGenetics