NeuroscienceStem Cell ReportsPeer-reviewed
Modelling and rescue of RP2 Retinitis Pigmentosa using iPSC Derived Retinal Organoids
Amelia Lane, Katarina Jovanovic, Ciara Shortall…·Michael E. Cheetham
This study uses iPSC-derived retinal organoids to model RP2 retinitis pigmentosa and shows that AAV-mediated gene augmentation can rescue photoreceptor degeneration.
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