NeurosciencebioRxivPreprint
GBA1 deficiency differentially affects endolysosomal trafficking in neurons versus astrocytes
Anna J. Park, Sarah Fish, Colby L. Samstag…·Marie Y. Davis
This study models GBA1 deficiency in neurons and astrocytes using iPSCs, revealing cell-type specific endolysosomal trafficking defects and -synucleinopathy in neurons, while astrocytes show neurotoxic reactivity.
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