Delivery of a chemically modified noncoding RNA domain improves dystrophic myotube function
Zeinabou Niasse‐Sy, Bo Zhao, Ajda Lenardič, Huyen Thuc Tran Luong, Ori Bar‐Nur, Johan H. Auwerx, Martin Wohlwend
This study identifies a pro-myogenic domain in CYTOR and shows that chemically modified RNA delivery improves dystrophic myotube function.
Advanced Science · Feb 17, 2025Peer-reviewedBioengineering