Molecular BiologybioRxivPreprint
Functional evaluation of a natural AAV capsid liver targeting motif in human hepatocytes
Carmen Unzu, Amanda X. Chen, Liliana Mâncio-Silva…·Luk H. Vandenberghe
The paper evaluates a natural AAV capsid liver targeting motif in human hepatocytes using in vivo and in vitro models, showing its role in liver targeting and the impact of PEG on transduction.
DOI 10.64898/2026.08.20.745184