Quantitative single-cell transcriptome-based ranking of engineered AAVs in human retinal explants
Z. Xi, B. E. Ozturk, M. E. Johnson, W. R. Stauffer, L. C. Byrne
This study ranks engineered AAVs in human retinal explants using single-cell RNA-Seq, identifying top-performing serotypes for retinal gene therapy.
bioRxiv · Sep 27, 2021Bioengineering