NeurosciencebioRxivPreprint
Mesenchymal Stromal Cell Therapeutic Potential to RestoreNeurovascular Integrity in Machado-Joseph Disease
Inês Barros, Daniela Gonzaga, Diana Lobo…·Catarina Oliveira Miranda
This study evaluates the therapeutic potential of mesenchymal stromal cells (MSC) in mitigating vascular abnormalities and blood-brain barrier (BBB) disruption in Machado-Joseph disease (MJD) transgenic mice, showing partial restoration of vascular and BBB integrity.
DOI 10.64898/2026.01.31.703043