PKM2 ablation enhanced retinal function and survival in a preclinical model of retinitis pigmentosa
Ethan Zhang, Joseph Ryu, Sarah R. Levi, Jin Kyun Oh, Chun Wei Hsu, Xuan Cui, Ting-Ting Lee, Nan‐Kai Wang, José Ronaldo Lima de Carvalho, Stephen H. Tsang
This study shows that PKM2 ablation improves photoreceptor survival and function in a preclinical RP model, suggesting metabolic reprogramming as a potential treatment.
Mammalian Genome · Apr 1, 2020Peer-reviewedGenetics