PathologybioRxivPreprint
Abca4 inhibition in a cone-rich rodent leads to Stargardt Disease type 1-like retinal degeneration
Fabiana Sassone, Michel Joseph Roux, Dominique Ciocca…·David Hicks
This study shows that Abca4 inhibition in a cone-rich rodent model leads to retinal degeneration similar to human Stargardt Disease type 1.
DOI 10.1101/2023.09.04.556201