Specific mutations in genes responsible for Alzheimer and for Duchenne Muscular Dystrophy introduced by Base editing and PRIME editing.
Joël Rousseau, Cedric Happi Mbakam, Antoine Guyon, Guillaume Tremblay, Francis-Gabriel Bégin, Jacques P. Tremblay
The paper evaluates base editing and PRIME editing techniques to introduce specific mutations in genes associated with Alzheimer's and Duchenne Muscular Dystrophy, assessing their efficiency in cell lines and potential therapeutic impact.
bioRxiv · Jul 31, 2020 · PreprintGenetics