iPS-CNM: an iPSC collection generated by base editing for centronuclear myopathy
Insa Staecker, Claudia Pommerenke, Amy Ellinghaus, Ida Steinkirchinger, Vivien Hauer, Hannah Kallnischkies, Maren Kaufmann, Lothar Groebe, Silke Fähnrich, Josephine Haake, Laura Steenpaß, Haicui Wang
The paper generates an iPSC collection with CNM mutations using base editing and evaluates off-target effects via whole genome sequencing.
bioRxiv · Sep 21, 2026 · PreprintGenetics