GeneticsbioRxivPreprint
iPS-CNM: an iPSC collection generated by base editing for centronuclear myopathy
Insa Staecker, Claudia Pommerenke, Amy Ellinghaus…·Haicui Wang
The paper generates an iPSC collection with CNM mutations using base editing and evaluates off-target effects via whole genome sequencing.
DOI 10.64898/2026.09.15.751756