Time-resolved FRET screening identifies small molecular modifiers of mutant Huntingtin conformational inflexibility in patient-derived cells
Johannes H. Wilbertz, Julia Frappier, Sandra Muller, Sabine Gratzer, Walter Englaro, Lisa M. Stanek, Barbara Calamini
The paper identifies small molecules that restore mutant Huntingtin conformational flexibility in patient-derived cells using a TR-FRET assay.
SLAS DISCOVERY · Jan 25, 2022Peer-reviewedNeuroscience