HDAC-6 inhibition ameliorates the early neuropathology in a mouse model of Krabbe disease
Sandra Bráz, Marlene M. Morgado, Marta Isabel Pereira, Ana Carolina Monteiro, Olga Golonzhka, Matthew B. Jarpe, Pedro Brites, Mónica Mendes Sousa, Joana Nogueira‐Rodrigues
This study shows that HDAC6 inhibition with ACY-738 improves early neuropathology and neuronal defects in a mouse model of Krabbe disease.
Frontiers in Molecular Neuroscience · Jul 27, 2023Peer-reviewedNeuroscience