PathologybioRxiv
Acitretin mitigates uroporphyrin-induced bone defects in congenital erythropoietic porphyria models
J. Bragazzi Cunha, J. S. Elenbaas, D. Maitra…·B. Omary
This study identifies acitretin as a potential treatment for congenital erythropoietic porphyria by mitigating uroporphyrin-induced bone defects in a zebrafish model.
DOI 10.1038/s41598-021-88668-9