BioengineeringbioRxivPreprint
CRISPR-Cas9 Engineered Extracellular Vesicles for the Treatment of Dominant Progressive Hearing Loss
X. Pan, P. Huang, S. Ali…·M. He
The paper develops a scalable microfluidic electroporation system to load gRNA:Cas9 RNP complexes into extracellular vesicles, achieving effective gene therapy for hearing loss in a mouse model.
DOI 10.1101/2023.09.14.557853