Intravenously Delivered Lipid Nanoparticles Access Acute Spinal Cord Injury via Disrupted Vasculature
Jacobus Burger, Luke J. Bolstad, Mia J. LaRico…·Daniel J. Hellenbrand
This study shows that intravenously delivered mRNA-lipid nanoparticles can access the injured spinal cord via disrupted blood-spinal cord barrier, achieving local transgene expression in multiple cell types.