Molecular BiologybioRxivPreprint
Targeted p63 isoform switch corrects dominant mutations in AEC syndrome without disrupting epidermal homeostasis
Daniela Di Girolamo, Gloria Urciuoli, Stefano Sol…·Caterina Missero
This study shows that switching to the p63{beta} isoform can correct AEC syndrome mutations in human keratinocytes without disrupting skin homeostasis.