PhysiologyMolecular TherapyPeer-reviewed
Neonatal systemic gene therapy restores cardiorespiratory function in a rat model of Pompe disease
David Dwight Fuller, Sabhya Denise Rana, Prajwal Pradeep Thakre…·Barry J. Byrne
4 citations
Author
Northwestern UniversityORCID 0000-0001-8634-9139Unclaimed ORCID profile · follow to get notified of new preprints
2 papers
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David Dwight Fuller, Sabhya Denise Rana, Prajwal Pradeep Thakre…·Barry J. Byrne
Ashlee M. Long, Jason M. Kwon, GaHyun Lee…·Elizabeth M. McNally
The paper shows that different forms of muscular dystrophy have distinct ECM compositions that affect myoblast motility, with annexin A6 playing a key role in enhancing movement.