PathologybioRxivPreprint
Periostin exon 17 skipping enhances the efficacy of local AAV-microdystrophin administration in a fibrotic model of Duchenne muscular dystrophy
Jessica Trundle, Alexis Boulinguiez, Ngoc Lu‐Nguyen…·Linda J. Popplewell
This study shows that periostin exon 17 skipping combined with AAV-microdystrophin improves muscle function and microdystrophin expression in a fibrotic DMD model.
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