GeneticsMolecular Therapy — Nucleic AcidsPeer-reviewed
In vivo base editing rescues photoreceptors in a mouse model of retinitis pigmentosa
Jing Su, Kaiqin She, Li Song…·Yang Yang
This study uses base editing to correct a Pde6b mutation in a mouse model of retinitis pigmentosa, restoring photoreceptor function and visual ability.
41 citations