AAV delivery of RNA editing machinery rescues SUDEP and seizure phenotype in a mouse model of Dravet Syndrome
Ellie M. Chilcott, Juan F. Antinao Diaz, Amanda Almacellas‐Barbanoj, Marc Moore, Anna Keegan, Zakary Waddington, Vicky Fang, Stéphanie Schorge, Gabriele Lignani, Simon N. Waddington, Rajvinder Karda
This study demonstrates that AAV-delivered RNA editing machinery improves survival and reduces seizures in a mouse model of Dravet Syndrome.
bioRxiv · Jul 18, 2025 · PreprintNeuroscience