NeurosciencebioRxivPreprint
Template-independent genome editing and repairing correct frameshift disease in vivo
Lian Liu, Kuan Li, Linzhi Zou…·Wei Xiong
This study demonstrates that NHEJ-mediated frame restoration can efficiently correct frameshift mutations in vivo, restoring function in a mouse model of Usher syndrome.
DOI 10.1101/2020.11.13.381160