Targeted blocking of gene splicing can dysregulate intron-embedded microRNAs
Md Hasan Ali, Wojciech Kwiatkowski, Piotr M. Kopec, Naveen Nedunchezhian, Sebastian Pęcherz, Natalia Kowalewska, Barbara Gnutti, Dario Finazzi, Savani Anbalagan
The paper shows that ASOs targeting splice sites can affect intronic microRNA expression and function, with implications for therapeutic strategies.
bioRxiv · Dec 4, 2024 · PreprintMolecular Biology