Molecular BiologybioRxivPreprint
Targeted blocking of gene splicing can dysregulate intron-embedded microRNAs
Md Hasan Ali, Wojciech Kwiatkowski, Piotr M. Kopec…·Savani Anbalagan
The paper shows that ASOs targeting splice sites can affect intronic microRNA expression and function, with implications for therapeutic strategies.
DOI 10.1101/2024.12.04.626772