NeurosciencebioRxivPreprint
VCAP-102 Achieves Exceptional BBB Penetration in Marmosets After Ten Years of AAV Capsid Evaluation
Yasunori Matsuzaki, Ayumu Konno, Yasuo Uchida…·Hirokazu Hirai
The paper evaluates BBB-penetrant AAV capsids in marmosets over a decade and identifies VCAP-102 as a superior candidate for systemic gene therapy.
DOI 10.64898/2025.12.06.692617