Myogenesis modelled by human pluripotent stem cells uncovers Duchenne muscular dystrophy phenotypes prior to skeletal muscle commitment
Virginie Mournetas, Emmanuelle Massouridès, Jean‐Baptiste Dupont, Étienne Kornobis, Hélène Polvèche, Margot Jarrige, Alan R.L. Dorval, Maxime R.F. Gosselin, Antigoni Manousopoulou, Spiros D. Garbis, Dariusz C. Górecki, Christian Pinset
This study uses hiPSCs from DMD patients to model myogenesis and identifies early disease phenotypes before skeletal muscle commitment.
Journal of Cachexia Sarcopenia and Muscle · Feb 1, 2021Peer-reviewedDevelopmental Biology