Author

Valentina Poletti

Harvard UniversityORCID 0000-0002-6886-1072Unclaimed ORCID profile · follow to get notified of new preprints

Biology Disciplines

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Genetics· 1 Neuroscience· 1

Signature Assays, Organisms & Methods

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Approach:experimental assay· 2 Organism:human· 1 Organism:mouse· 1

Frequent Co-Authors

Alessandra BiffiiD· 1 shared Ana Zguro· 1 shared Annarita MiccioiD· 1 shared Anne ChalumeauiD· 1 shared Cécile MassoniD· 1 shared Eleonora CavalcaiD· 1 shared Fulvio MavilioiD· 1 shared Giuliana FerrariiD· 1 shared

Activity by Year

2022-2023 · peak 1/yr

Co-Author Collaboration Network

10 top collaborators · 20 mutual co-author links

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1 shared paperNeuroscience

Alessandra BiffiORCID

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2 papers

Recent·Most cited

NeuroscienceEMBO Molecular MedicinePeer-reviewedMar 6, 2023

An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model

Marco Peviani, Sabyasachi Das, Janki Patel…·Alessandra Biffi

This study demonstrates that gene therapy using hematopoietic stem cells can mitigate CLN1 disease symptoms in mice, with enhanced benefits from hPPT1 overexpression and combined transplantation approaches.

10 citations

mouseexperimental assay

𝕏 PostBluesky

GeneticsbioRxivPreprintDec 31, 2022

Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies

Mégane Brusson, Anne Chalumeau, Pierre Martinucci…·Annarita Miccio

This study develops a bifunctional lentiviral vector for sickle cell disease that combines gene addition and gene silencing to reduce HbS levels and improve treatment efficacy.

2 citations

humanexperimental assay

𝕏 PostBluesky