Molecular BiologyMolecular Therapy — Nucleic AcidsPeer-reviewed
Improving angiogenesis ameliorates the efficacy of ASO-based exon-skipping for the treatment of Duchenne muscular dystrophy
Mathilde Blitek, Cécile Gastaldi, Mathilde Doisy…·Aurélie Goyenvalle
This study shows that improving angiogenesis enhances ASO-based exon-skipping therapy in DMD by increasing ASO delivery and dystrophin expression in mdx mice.
2 citations