Administration of barcoded AAV capsid library to the putamen of non-human primates identifies variants with efficient retrograde transport
Yulia Dzhashiashvili, Jodi L. McBride, Emily B. Fabyanic, Xin Huang, Brian M. Kelly, Greglynn D Walton-Gibbs, Vimala Vemireddi, Joan R. Wicks, Mohamad Nayal, Ariel A. Hippen, Zhenming Yu, Pichai Raman, Elizabeth A. Ramsburg, Marcus Davidsson, Esteban A. Engel, Tomas Björklund
The paper tests AAV capsid variants in non-human primates to identify those with improved retrograde transport properties.
Molecular Therapy · Dec 10, 2025Peer-reviewedNeuroscience