Lipid nanoparticle-mediated CRISPR/Cas9 delivery enables efficient trabecular meshwork gene editing in mice
Yifan Huang, Silin Pang, Linxian Li, Chi Wai Do, Qian Luo, 郑宗立, Wenjun Xiong
This study demonstrates that lipid nanoparticle-mediated CRISPR/Cas9 delivery efficiently edits genes in the trabecular meshwork of mice, inducing glaucoma-like features.
Journal of Controlled Release · Dec 2, 2025Peer-reviewedNeuroscience