Molecular BiologyJournal of Cystic FibrosisPeer-reviewed
FDA-Approved Drug Screening in Patient-Derived Organoids Demonstrates Potential of Drug Repurposing for Rare Cystic Fibrosis Genotypes
Eyleen de Poel, Sacha Spelier, Marne C. Hagemeijer…·Jeffrey Matthijn Beekman
The paper screens 1400 FDA-approved drugs in CF patient-derived intestinal organoids using a functional assay to identify potential repurposing for rare CF genotypes.
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